SIGN UP FOR UPDATES!
Sign up for Englemed updates from TwitterSign up for Englemed updates from Facebook
ENGLEMED
Contact Englemed
Our contact email address.
We can provide a specialist, tailored health and medical news service for your site.
Click here for more information
RSS graphic XML Graphic Add to Google
About Englemed news services - services and policies.
Englemed News Blog - Ten years and counting.
Diary of a reluctant allergy sufferer - How the British National Health Service deals with allergy.
BOOKS AND GIFTS THIS WAY!
BookshopFor books on women's health, healthy eating ideas, mental health issues, diabetes, etc click here
SEARCH THIS SITE
Copyright Notice. All reports, text and layout copyright Englemed Ltd, 52 Perry Avenue, Birmingham UK B42 2NE. Co Registered in England No 7053778 Some photos copyright Englemed Ltd, others may be used with permission of copyright owners.
Disclaimer: Englemed is a news service and does not provide health advice. Advice should be taken from a medical professional or appropriate health professional about any course of treatment or therapy.
FreeDigitalPhotos
www.freedigitalphotos.net
FreeWebPhotos
www.freewebphoto.com
FROM OUR NEWS FEEDS
Premature birth needs to be in specialist centres - study
Thurs October 17th - Women facing premature labour should be enabled to give birth in hospitals with specialist neonatal intensive care units, researchers say today. More
How GPs can respond to private gene test results
Thurs October 17th - Doctors confronted by patients armed with the results of private gene testing should check for family genetic history that might support the claimed results, according to experts today. More
RECENT COMMENTS
On 08/02/2018 David Kelly wrote:
Would you like to write a piece about this to be i... on Researchers unveil new pain re...
On 23/10/2017 Cristina Pereira wrote:
https://epidemicj17.imascientist.org.uk/2017/06/21... on HIV breakthrough - MRC...
On 12/09/2017 Aparna srikantam wrote:
Brilliant finding! indeed a break through in under... on Leprosy research breakthrough...
On 01/07/2017 Annetta wrote:
I have been diagnosed with COPD for over 12 years.... on Seaweed plan for antimicrobial...
On 12/03/2017 Steph wrote:
The photo you have paired with this article is its... on 'Fat shaming' limits...
BOOKS ON CHILDREN'S HEALTH
For books, child safety and gift ideas click here
NEWS FEEDS
ENGLEMED HEALTH NEWS

Gene treatment may cure children

Thursday August 25th, 2011

A trial of gene therapy on children with severe immune disorders has proved remarkably successful, British researchers reported last night.

Some 16 children underwent the children nine years ago and all are still alive, researchers at University College London and Great Ormond Street Hospital reported.

Even better, 14 of the children are living normal lives, researchers said.

The success of the trial was reported in Science Translational Medicine. The children had two kinds of severe combined immunodeficiency disorder - SCID, one called SCID-XI and one called ADA-SCID.

Until recently the diseases were regarded as incurable and children kept shielded from the outside world to prevent infection. Then treatments were developed using stem cell transplants with some success - but not all children could be saved.

The researchers say gene therapy seems to be more effective than stem cell transplants.

Researcher Professor Bobby Gaspar said the project was among a "handful" of studies" showing that gene therapy can work.

He said: "These children are going to school, attending parties doing everything other children are able to do.

"That's why it is exciting. we have two conditions and 14 children showing that gene therapy can be both successful and long-lasting."

He said gene therapy would offer something "different" if stem cell transplants were unlikely to work or a donor could not be found.

Long-Term Persistence of a Polyclonal T Cell Repertoire After Gene Therapy for X-Linked Severe Combined Immunodeficiency. H.B.Gaspar; S. Cooray; K.C. Gilmour; K.L. Parsley; S.J. Howe; J. Bayford; L. Brown; E. G. Davies; C. Kinnon; A.J Thrasher at University College London in London, UK; H.B. Gaspar; S. Cooray; K.C. Gilmour; K.L. Parsley; S. Adams; J. Bayford; L. Brown; E.G. Davies; A.J. Thrasher at Great Ormond Street Hospital NHS Trust in London, UK; A. Al Ghonaium at King Faisal Specialist Hospital and Research Centre in Riyadh, Saudi Arabia. Science Translational Medicine August 24 2011

Tags: Child Health | Genetics | UK News

Printer friendly page Printer friendly page

CATEGORIES